Williams Syndrome

Developmental disorder characterised by:

Epidemiology and Risk Factors

Prevalence of 1:~7,500.

Pathophysiology

Genetic condition that is:

  • Classified as autosomal dominant
  • Involves deletion of 26-28 genes on chromosome 7
    • The ELN gene encodes tropoelastin, which is involved in vascular wall development

Clinical Manifestations

Key characteristics:

  • Distinctive facies
    • Broad forehead
    • Epicanthal folds
    • Short nose
    • Long philtrum
    • Wide mouth
    • Thick vermillion
    • Mandibular hypoplasia
  • Developmental delay
  • Hypotonia
  • Hypercalcaemia
    Develops in infancy and resolves by ~4; unclear cause.
  • Cardiac disease
    • Present in 80%
      40% will require procedural intervention.
    • Includes
      • Supravalvular AS
        Non-compliant aorta narrows at the sinotubular junction, and ↑ AV leaflet degeneration. Severity usually remains stable in most patients.
      • Pulmonary artery stenosis
        Often occurs with SVAS.

Diagnostic Approach and DDx

Investigations

Bedside:

  • ECG:
    • LVH
    • Long QT
  • TTE:
    • Presence of AS
    • Presence of PS

Imaging:

  • Cardiac MRI

Management

Anaesthetic Considerations

  • A
    • Potentially difficult airway
      Secondary to mandibular hypoplasia.
  • C
    • Evaluate cardiac disease
      • Supravalvular AS
      • Coronary occlusion
    • 5-lead ECG
    • Defend coronary blood flow
      • Minimise NPO time
      • Maintain volume state
      • Avoid fall in SVR/ in PVR
  • F
    • Hypercalcaemia
      Testing recommended every 2 years.

Marginal and Ineffective Therapies

Complications

Include:

  • Perioperative death
    Likely due to myocardial ischaemia.

Prognosis

Key Studies


References

  1. Genetics Home Reference. Williams Syndrome. National Library of Medicine. 2019.
  2. Matisoff AJ, Olivieri L, Schwartz JM, Deutsch N. Risk assessment and anesthetic management of patients with Williams syndrome: a comprehensive review. Thomas M, ed. Paediatr Anaesth. 2015;25(12):1207-1215. doi:10.1111/pan.12775